Glucocerebrosidase (trade name Ceredase)

An enzyme used in treatment of inherited Gaucher’ s disease in which there is abnormal deposition of glucocerebrosides (hydrophobic lipid molecules that contain a hydrophilic sugar head group). Gaucher’ s disease is an enzyme deficiency disease that may be amenable to cure by incorporation of the gene coding for glucocerebrosidase into the patient’s genome via gene delivery techniques.


 


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